(Q38093778)

28 August 2017

title

Statistical challenges in the evaluation of treatments for small patient populations (English)

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28 August 2017

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3

Boris Freidlin

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28 August 2017

Edward L Korn

1

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28 August 2017

Lisa M McShane

series ordinal

2

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28 August 2017

language of work or name

English

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publication date

1 March 2013

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Science Translational Medicine

28 August 2017

published in

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28 August 2017

volume

5

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28 August 2017

issue

178

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28 August 2017

page(s)

178sr3

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Effect of VX-770 in persons with cystic fibrosis and the G551D-CFTR mutation

28 August 2017

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A general inefficacy interim monitoring rule for randomized clinical trials

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Role of independent data-monitoring committees in randomized clinical trials sponsored by the National Cancer Institute

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21 January 2018

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21 January 2018

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21 January 2018

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21 January 2018

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21 January 2018

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21 January 2018

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Imatinib compared with interferon and low-dose cytarabine for newly diagnosed chronic-phase chronic myeloid leukemia

21 January 2018

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De novo CIAS1 mutations, cytokine activation, and evidence for genetic heterogeneity in patients with neonatal-onset multisystem inflammatory disease (NOMID): a new member of the expanding family of pyrin-associated autoinflammatory diseases

21 January 2018

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Chronic infantile neurological cutaneous and articular syndrome is caused by mutations in CIAS1, a gene highly expressed in polymorphonuclear cells and chondrocytes

21 January 2018

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21 January 2018

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21 January 2018

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Much ado about not...enough data: high-dose chemotherapy with autologous stem cell rescue for breast cancer

21 January 2018

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21 January 2018

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The Will Rogers phenomenon. Stage migration and new diagnostic techniques as a source of misleading statistics for survival in cancer

21 January 2018

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21 January 2018

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21 January 2018

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21 January 2018

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21 January 2018

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21 January 2018

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21 January 2018

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21 January 2018

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21 January 2018

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21 January 2018

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21 January 2018

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21 January 2018

Identifiers

DOI

1 reference

28 August 2017

1 reference